3 drugs for “Thalassemia”

Phase 3 3

  • CTX001VERTEX PHARMACEUTICALS INCBeta-Thalassemia; Thalassemia
  • EtavopivatNOVO NORDISK A SThalassemia
  • Mitapivat matchedAGIOS PHARMACEUTICALS, INC.Transfusion-dependent Alpha-Thalassemia; Transfusion-dependent Beta-Thalassemia

Drugs whose recorded indications name this term, by development stage. Indications come from registries and labels, so a drug can appear under related terms.